A scientific article by Ms. Nour al-Huda Azmi Hassan entitled: Gene Editing Technology for Treating Genetic Diseases

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CRISPR-Cas9 technology is considered a "Copernican Revolution" in modern medicine, granting scientists the ability to edit the "Catalog of Life" with extreme precision. The idea is based on using the (Cas9) protein as "Molecular Scissors" and a guide molecule that directs it to a specific sequence within the DNA. Upon reaching the target, the damaged part or the mutation causing the genetic disease is cut, allowing the cell to either disable the disease-causing gene or use a "healthy template" to repair the defect. This technology is currently being used to treat diseases once thought impossible, such as "Sickle Cell Anemia," by modifying the patient's blood stem cells and re-transplanting them. It also opens horizons for treating "Muscular Dystrophy" and correcting mutations causing "Cystic Fibrosis" in the lungs. Despite these hopes, the technology sparks wide debate regarding "Bioethics," especially concerning the editing of "embryos" and its impact on future generations. The ultimate goal of gene editing is to transition from "symptom management" to the "radical eradication" of diseases from the human genetic code, ensuring a healthy life for individuals born with previously destined genetic defects.
  الهدف الرابع : التعليم الجيد